Publications “An integrated modelling methodology for estimating the prevalence of centronuclear myopathy” “An integrated modelling methodology for estimating global incidence and prevalence of hereditary spastic paraplegia subtypes SPG4, SPG7, SPG11, and SPG 15” Posters “Drug Development: Meeting Future Societal Requirements Converting Outcome Data into Inputs for Cost-Effectiveness Models” “Aligning Drug Development with Future Patient-Centric Market Access (PACEMA) requirements” “Long-term durability in cost-effectiveness models of gene therapies: Review of Health Technology Assessment cases” “An integrated modelling methodology for estimating global, regional, and country-specific incidence and prevalence of Tay-Sachs Disease at subtype level”Full references’ list supplement
